News

Hemispherian Receives U.S. FDA Orphan Drug Designation for GLIX1 for the Treatment of Malignant Glioma
Hemispherian AS, a pioneering biotech company developing next-generation therapeutics for aggressive cancers, announced today that the U.S. Food and Drug Administration (FDA) has granted Orphan Drug ...
Medical Dialogues3h
Sanofi Riliprubart receives orphan drug designation in Japan for chronic inflammatory demyelinating polyneuropathy
Paris: Sanofi has received orphan drug designation from the Ministry of Health, Labour and Welfare (MHLW) in Japan for ...
Parliamentarian reverses course on rare disease drug price provision in tax bill
The Senate Parliamentarian reversed course on a small provision in the One Big Beautiful Bill Act that could boost cures for rare diseases.
Texas increases well plugging budget as backlog of orphan sites grows
The Railroad Commission’s program for sealing orphan oil and gas wells will get an additional $100 million over the next two ...
Proof-of-Concept Results Show Jaguar Health’s Crofelemer Reduced Total Parenteral Nutrition in Third Intestinal Failure Orphan Disease Patient
As recently announced, initial proof-of-concept results from this ongoing investigator-initiated trial (IIT) show crofelemer ...
I won the ‘orphan lottery’ in Russia and Canada transformed my life: ‘If you hadn’t been adopted, you’d be on the streets. Or dead.'
My story began at Baby House No. 1 in Novosibirsk, Russia, one of thousands of children left behind in the wake of the Soviet ...
‘If you hadn’t been adopted, you’d be on the streets. Or dead': I won the ‘orphan lottery’ in Russia and Canada transformed my life
My story began at Baby House No. 1 in Novosibirsk, Russia, one of thousands of children left behind in the wake of the Soviet ...
WOUB Public Media16h
Orphan wells pose a threat to groundwater in Ohio
Scientists recently released research showing where groundwater is most at risk of contamination by orphan wells.
Fierce Pharma17h
Orphan Cures Act re-added to Trump tax bill as Senate prepares to begin vote-a-rama
The Orphan Cures Act has been added back into the Senate version of President Donald Trump’s “big, beautiful bill” after being ...
The Statehouse News Bureau22h
Orphan wells pose threat to groundwater in Ohio
The Appalachian Basin – which includes parts of eastern Ohio – is one of the areas where aquifers are most at risk.
Sanofi: Riliprubart granted orphan drug designation in Japan for chronic inflammatory demyelinating polyneuropathy
Riliprubart granted orphan drug designation in Japan for chronic inflammatory demyelinating polyneuropathy Two phase 3 studies are currently underway testing riliprubart in people with CIDP as ...
The Manila Times1d
Press Release: Riliprubart granted orphan drug designation in Japan for chronic inflammatory demyelinating polyneuropathy
Riliprubart granted orphan drug designation in Japan for chronic inflammatory demyelinating polyneuropathy. Two phase 3 studies are currently underway testing riliprubart in peopl ...